Communiqué de presse : Le venglustat de Sanofi a atteint tous les critères d'évaluation principaux dans une étude de phase 3 sur la maladie de Gaucher de type 3
View original at globenewswire.comCommuniqué de presse : Le venglustat de Sanofi a atteint tous les critères d'évaluation principaux dans une étude de phase 3 sur la maladie de Gaucher de type 3 Le venglustat de Sanofi a atteint tous les critères d'évaluation principaux dans une étude de phase 3 sur la maladie de Gaucher de type 3 Dans l’étude de phase…
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Venglustat was generally well tolerated with no new safety signals compared to previous studies
80% confidenceVenglustat achieved equivalent performance to enzyme replacement therapy on non-neurological criteria including spleen volume, liver volume, and hemoglobin levels
80% confidenceThese results underscore Sanofi's commitment to rare disease research and desire to offer new perspectives to people living with these conditions
80% confidenceA daily pill could make a considerable difference for Gaucher disease patients facing neurological challenges
80% confidencePERIDOT study showed pain reduction in both study arms and did not meet the primary endpoint
80% confidenceVenglustat demonstrated statistically significant improvements in neurological symptoms (p=0.007) compared to enzyme replacement therapy at week 52
80% confidenceThere is currently no approved treatment for the neurological manifestations of GD3
80% confidence
Data points we hold from this source
| Sanofi · rare disease experience | 40 years |
